While Denali plans to submit tivi for accelerated approval early this year, the company is also continuing its investigation of the drug in an ongoing phase 2/3 double-blind, randomized trial in ...

BEDFORD, Mass., Feb. 22, 2023 (GLOBE NEWSWIRE) -- Homology Medicines, Inc. (Nasdaq: FIXX), a genetic medicines company, announced today the presentation of preclinical data that supports the ...

Adults with Down syndrome often develop chronic health problems, such as severe sleep apnea, digestive disorders, thyroid conditions, and obesity. Many develop Alzheimer’s disease in middle age.

When Hunter syndrome affects the brain, which is about 75% of the time, symptoms usually show up between 18 months and 4 years of age. They start about 2 years later when the disease is milder.

Because these adults are at greater risk than the general population, Chicoine added, a lot of current research focuses on detection and prevention of Alzheimer’s in the Down syndrome community.

The life expectancy for people with Down syndrome has increased dramatically, but now, aging adults with the condition face a health system unprepared to care for them.