Duchenne muscular dystrophy occurs when that gene fails ... These may include: Muscle biopsy. A small piece of muscle tissue is removed and examined to confirm the diagnosis or rule out another ...

Contrary to prior data, this study shows that neither eosinophils nor STAT6-mediated IL-4/IL-13 signaling contribute ...

Duchenne muscular dystrophy (DMD) is a genetic condition that causes progressive muscle weakness and wasting. It is an X-linked recessive disorder that occurs due to changes in the DMD gene ...

McGill researchers discovered that K884, an experimental drug, enhances muscle stem cell repair in Duchenne muscular dystrophy (DMD). Unlike gene therapies, K884 targets DMD-affected cells regardless ...

While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...

BOSTON - Entrada Therapeutics , Inc. (NASDAQ:TRDA) received authorization from the UK's Medicines and Healthcare Products Regulatory Agency (MHRA) to initiate a Phase 1/2 clinical trial for its ...

The prevalence of Duchenne muscular dystrophy is 1 in 35,000 males. [12] The prevalence of pervasive developmental disorder in the male population is 1.6 in 1000, approximately four times more ...

Muscular Dystrophy (MD) is a genetic condition causing progressive muscle weakness and complications in vital organs. Early diagnosis, multidisciplinary care, and emerging treatments like gene therapy ...

Sarepta Therapeutics has decided not to continue the development of vesleteplirsen, a follow-up to its Duchenne muscular dystrophy (DMD ... the population with the muscle-wasting disease.

What Is Duchenne Muscular Dystrophy? Muscular dystrophies are a ... your child might have other symptoms, including: The muscle problems can cause cramps at times, but in general, DMD isn ...

We hypothesize that Duchenne muscular dystrophy and autism spectrum disorder/pervasive developmental disorder co-occur with a greater than random frequency. In this study, we set out to reject the ...