Researchers have described the neurodegeneration that occurs in the nervous system of the bowel in Batten disease, a rare and fatal genetic condition. In their latest study, a team showed that gene ...
With an FDA approval submission for RegenXBio’s Hunter syndrome gene therapy already underway, the biopharma has now ...
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Regenxbio and Nippon Shinyaku forge $810m gene therapy dealRegenxbio will receive $110m upfront from Nippon Shinyaku and is eligible to get up to $700m in development, regulatory, and ...
Data from the first patients enrolled into Regenxbio's trial of its gene therapy for rare inherited disease mucopolysaccharidosis type I (MPS I) – also known as Hurler syndrome – has shown the ...
Regenxbio, a prolific developer of gene therapy technology, will hand Japan’s Nippon ... The other treatment, RGX-111, treats ...
Giving gene therapy to newborn mice with Batten disease ... and similar neurodegenerative conditions in children such as the mucopolysaccharidoses, another group of rare inherited diseases caused ...
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