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Project Alive Shines a Light on Rare Disease Week and Rare Disease Day to Raise Awareness for Hunter Syndrome
This annual observance brings attention to the 300 million people worldwide living with rare diseases, including those impacted by Hunter syndrome. Rare Disease Week, held in conjunction with Rare ...
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GC Biopharma designates Hunter syndrome treatment as orphan drug in South Korea
GC Biopharma announced on the 5th that the Ministry of Food and Drug Safety has designated the treatment for severe Hunter syndrome, 'Hunterase ICV (intracerebroventricular),' as an orphan drug.
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Denali Therapeutics Announces Primary Analysis and Long-Term Follow-Up of Phase 1/2 Study in Hunter Syndrome (MPS II) with Tividenofusp Alfa
Feb. 06, 2025 (GLOBE NEWSWIRE) -- Denali Therapeutics Inc. (NASDAQ: DNLI), today announced the primary analysis of the Phase 1/2 study in 47 participants with Hunter syndrome (MPS II) in the 24-week ...