Left: Muscle fibers expressing dysferlin (purple) made from gene-edited muscle stem cells transplanted ... are developing a targeted treatment for muscular dystrophy with the help of gene-editing.

The dysferlin protein is primarily responsible for repairing cell membranes ... successfully removed muscle stem cells from two patients with limb-girdle muscular dystrophy, corrected the genetic ...

Ips Heart Inc. has been awarded orphan drug designation by the FDA for its GIVI-MPC stem cell therapy for Becker muscular dystrophy. GIVI-MPC has the unique ability to create new muscle with full ...

Stem cell therapy is yet to prove effective for muscular dystrophy and has not been approved on the NHS so Celine's parents, Lottie and Charlie, have instead raised £86,000 to fund the treatment ...

FSHD is the second most common form of muscular dystrophy after the Duchenne type, and affects around 1 million people worldwide, with no approved treatments ... large B-cell lymphoma (DLBCL).

Muscular Dystrophy (MD) is a genetic condition causing progressive muscle weakness and complications in vital organs. Early ...

IPS HEART has now shown GIVI-MPCs create new human muscle with full length human dystrophin in dystrophic pigs, young and extremely aged Duchenne Muscular Dystrophy (DMD) mice and in a sarcopenia ...

Lack of muscle stem cell targeting limits the treatment of muscular dystrophies ... Dysferlin-deficient muscular dystrophy is a devastating and untreatable disease. Using Cas9, the authors ...

An Irish woman has launched a fundraiser to help raise money for medical treatment for her seven-year-old son. Una Ennis' son ...