Left: Muscle fibers expressing dysferlin (purple) made from gene-edited muscle stem cells transplanted ... are developing a targeted treatment for muscular dystrophy with the help of gene-editing.

A novel drug holds promise for treating Duchenne muscular dystrophy (DMD), a rare ... the natural repair abilities of muscle stem cells. Current treatments can slow muscle damage, but don ...

Current treatments can slow muscle damage ... PTPN1/2 inhibition promotes muscle stem cell differentiation in Duchenne muscular dystrophy. Life Sci Alliance. 2025;8(1):e202402831. doi: ...

Ips Heart Inc. has been awarded orphan drug designation by the FDA for its GIVI-MPC stem cell therapy for Becker muscular dystrophy. GIVI-MPC has the unique ability to create new muscle with full ...

Muscular Dystrophy (MD) is a genetic condition causing progressive muscle weakness and complications in vital organs. Early ...

The dysferlin protein is primarily responsible for repairing cell membranes ... successfully removed muscle stem cells from two patients with limb-girdle muscular dystrophy, corrected the genetic ...

Stem cell therapy is yet to prove effective for muscular dystrophy and has not been approved on the NHS so Celine's parents, Lottie and Charlie, have instead raised £86,000 to fund the treatment ...

An Irish woman has launched a fundraiser to help raise money for medical treatment for her seven-year-old son. Una Ennis' son ...

IPS HEART has now shown GIVI-MPCs create new human muscle with full length human dystrophin in dystrophic pigs, young and extremely aged Duchenne Muscular Dystrophy (DMD) mice and in a sarcopenia ...

Satellos has invented SAT-3247 as a first-of-its-kind, orally administered small molecule drug designed to restore skeletal muscle regeneration initially in Duchenne muscular dystrophy (DMD).