Richard Engel and his wife Mary are taking their son Henry Thomas‘ Rett syndrome diagnosis day ... with “redoubling her efforts in physical therapy” for Henry, calling her a “tough woman ...

Neurogene has halted patient enrolment in the high-dose arm of its trial of Rett syndrome gene therapy, sparking another run on its shares. Last week, the company reported that NGN-401 had shown ...

Neurogene has reported encouraging efficacy results with its gene therapy for rare genetic disorder Rett syndrome, but investors' concerns about safety seem to be weighing on its share price.

Rett Syndrome is a rare genetic neurological ... a stay-at-home mom who currently engages her son in up to seven forms of physical therapy a week, in order to help him advance physically and ...