Dan was so small when he was born that his owner "could barely tell there was a puppy" inside the amniotic sac and he needed ...

TYRA-300 is the only orally administered investigational agent in clinical development for IR NMIBC- -Initial 3-month complete response (CR) data expected to be reported ...

Health state utility values (HSUVs) for achondroplasia were consistently lower than normative population values, with complications in adolescence and adulthood producing the most pronounced ...

"Our research suggests that PDE3 inhibitors could be repurposed for treating conditions characterized by short stature, such as achondroplasia or idiopathic short stature," add Dr. Ichimura and ...

At the start of June, Grow a Garden launched a Bizzy Bees Event, where friendly pollinators can bring a new mutation to your plants. However, there is also an ...

Ascendis Pharma A/S (NASDAQ:ASND) is among the 13 Biotech Stocks with Huge Upside Potential. It reported interim Week 26 data from its Phase 2 COACH Trial, confirming that combining TransCon hGH ...

Ascendis Pharma has reported week 26 interim analysis outcomes from the ongoing Phase II COACH Trial assessing combo treatment using TransCon CNP (navepegritide) and TransCon hGH (lonapegsomatropin) ...

The Food and Drug Administration (FDA) has accepted for Priority Review the New Drug Application (NDA) for TransCon ® CNP (navepegritide) for the treatment of children with achondroplasia, a rare ...

Caring for a child with achondroplasia imposes a significant social and emotional burden on parents, according to results published in Frontiers in Medicine. A narrative review of parental outcomes ...

Protein redesign is an enzyme engineering strategy that enhances a template enzyme’s properties by introducing mutations. Although the method is broadly employed for enzyme design, finding optimal ...

Craniometaphyseal dysplasia (CMD) is a bone dysplasia characterized by overgrowth and sclerosis of the craniofacial bones and abnormal modeling of the metaphyses of the tubular bones. Hyperostosis ...