The Muscular Dystrophy Association (MDA) has selected Lily Sander from Charlotte, North Carolina, as its 2025 MDA National Ambassador. Sander joins MDA National Ambassador Ira Walker from Fort ...

The FDA has granted fast track designation to DYNE-101, a therapy for myotonic dystrophy type 1 (DM1) now in testing in a ...

We are pleased to announce that our applications for the higher dose regimen of nusinersen are now under review in the US and Europe,” said Stephanie Fradette, Pharm.D., Head of the Neuromuscular ...

The symptoms of myotonic dystrophy may be obvious from birth or they can develop later -- during the teenage or adult years. Like other forms of muscular dystrophy, myotonic dystrophy leads to ...

What Is Duchenne Muscular Dystrophy? Muscular dystrophies are ... The disease almost always affects boys, and symptoms usually begin early in childhood. Children with DMD have a hard time standing ...

In August 1985, I was diagnosed with Becker muscular dystrophy. So the doctors focused on the Becker type, as the majority of my presenting symptoms were similar to Duchenne’s. These included having ...

Early onset IBD activity correlates with higher psychiatric ... From this database, the researchers identified all adult patients newly diagnosed with IBD and who had documented IBD-specific ...

Jeffrey Donald Carcic, age 62, passed away due to complications of Adult-Onset Myotonic Muscular Dystrophy late in the evening on Tuesday, January 7, 2025. He was born on February 13, 1962 ...

In the case of limb-girdle muscular dystrophy, muscle deterioration is progressive and young adults lose the ability to walk and normal use of their arms and hands. “You go from being a good athlete ...

Six in 10 adults put the early signs of dementia down to old age rather than the condition itself, with common symptoms like misplacing items and needing help with everyday tasks getting mixed up.

A Phase 3 clinical trial investigating Elevidys (delandistrogene moxeparvovec), a gene therapy for Duchenne muscular dystrophy, did not achieve its primary endpoint, according to findings ...