They were told their baby would die before she turned three. How did she defy the odds?
On her most recent birthday, Jess Schonberger woke to the sounds of joy. In her balloon-festooned Sydney bedroom, her ...
pharmaphorum2d
Pfizer buys gene therapy firm Bamboo
Bamboo has pre-clinical treatments for Duchenne muscular dystrophy, Friedreich’s Ataxia and Canavan disease, and a phase 1 asset for Giant Axonal Neuropathy. Unlike Biogen and its investment of ...
News Medical6d
Preclinical MRI for neurological diseases with cellular and molecular imaging
For instance, serial MRI and MRS were utilized to track adeno-associated virus-mediated gene delivery therapy in a mouse model of Canavan disease. 9 In aspartoacylase (ASPA)- deficient lacZ-knock ...
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Is This Biotech Stock With 150% Upside a Buy Now?
Plus, BBP-812 is in a Phase ½ clinical trial for adeno-associated virus gene therapy for Canavan disease. While BridgeBio’s prospects look promising, investors should be aware of the risks ...
Independent.ie7d
Cuala are All-Ireland club SFC champions: As it happened
It’s All-Ireland club finals days at Croke Park with Errigal Ciaran and Cuala facing off in the football for the Andy ...
Irish Daily Mirror6d
First-half collision that forced Darragh Canavan out of the All-Ireland final
You can check out at any time. More info Darragh Canavan was taken to the Mater hospital to get checked out after being caught by an opponent in a tussle for possession during the All-Ireland club ...