Learning from examples like congenital heart disease and cystic fibrosis can help health systems and clinicians prepare to care for an influx of patients with neuromuscular diseases as they reach ...
Posters presented at the 2025 Muscular Dystrophy Association Clinical & Scientific Conference highlight the complex care ...
A grandmother joined her son and some family friends to abseil 100 feet down from the Falkirk Wheel to raise vital cash for ...
Sarepta Therapeutics (SRPT) stock is reeling this week following the death of a 16-year-old patient treated with its flagship gene therapy, ...
An Indiana man is proving that determination can break down barriers by starting his own company despite life's challenges.
The sky is the limit for Co Antrim pilot Matthew Monaghan who has refused to take no for an answer his entire life after ...
Rare diseases - a medical condition so obscure that even your doctor has to Google. Despite their name, these diseases ...
Taking her family’s struggle with a terminal illness and creating a non-profit to help others going through the same ...
St. Anthony’s Memorial Hospital already offers many pediatric therapy services to care for children with diagnoses such as ...
The young man died of acute liver injury, a known side effect, Sarepta said in a statement. But the company said the ...