Danon disease is a rare genetic disorder primarily caused by mutations in the LAMP2 gene, which is crucial for the proper functioning of lysosomes—organelles responsible for breaking down waste ...

Rocket’s RP-A501 for Danon disease has potential to be a $1B commercial opportunity, the analyst tells investors in a research note. The firm thinks an accelerated approval pathway may be ...

Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT) stock has hit a 52-week low, dropping to $10.11, as the company faces a ...

John Militello, Vice President of Finance and Treasurer at Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT), recently sold 896 ...

AR inheritance in a patient with cardiomyopathy due to Friedreich disease or X linked inheritance in Fabry or Danon disease). Genetic testing may also be helpful to clarify the diagnosis in borderline ...

Israel, backed by Washington, will cease contact with the UN's Palestinian humanitarian relief agency UNRWA and any body ...

Donald Trump is remaking the traditional boundaries of Washington, unleashing unprecedented executive orders and daring ...

Neither Danon nor Netanyahu have specified what the ... Hostages in Hamas captivity will remain at risk of dying from starvation, disease and violence at the hands of Hamas fighters (or dying ...

Fighting destroyed hospitals and sparked outbreaks of infectious disease, while hundreds of thousands ... in Jerusalem," the Israeli envoy, Danny Danon, told the UN Security Council.