After Sarepta reported the death of a patient who had recently taken the gene therapy Elevydis, patient advocacy group Parent ...

A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...

The young man died of acute liver injury, a known side effect, Sarepta said in a statement. But the company said the ...

Opens in a new tab or window Share on LinkedIn. Opens in a new tab or window The initial signs of Duchenne muscular dystrophy in a 3 or 4-year-old child may be subtle, explains Dr. Alexandra ...

A young man treated with Elevidys died of acute liver failure. The case may give doctors pause before prescribing the ...

Sarepta Therapeutics said that a young man died after receiving Elevidys, its gene therapy for Duchenne muscular dystrophy ...

REGENXBIO (RGNX) reported new, positive interim data from two additional patients in the Phase I/II portion of the AFFINITY DUCHENNE trial of ...

European regulators are to review Sarepta Therapeutics’ Duchenne muscular dystrophy drug, eteplirsen – a drug that has sparked controversy in the US, where it was approved by the FDA against ...

Eight-year-old Sam Millar has a condition called Duchenne muscular dystrophy, a genetic muscle-wasting disease that progressively gets worse over time. He is a statistical outlier – Duchenne UK says ...

Muscular endurance is a muscle's ability to complete multiple repetitions ("reps") of a movement against resistance for an extended period. Muscular endurance improves athletic performance and the ...