After Sarepta reported the death of a patient who had recently taken the gene therapy Elevidys, patient advocacy group Parent ...
Clinical Trials Arena on MSN1d
Regenxbio’s DMD gene therapy drives 122.3% biomarker uptick in three-year-oldThe interim data found one child in the Duchenne trial produced more than double the amount of the protein needed to maintain ...
A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...
A patient has died while taking a closely watched gene therapy for muscular dystrophy. Sarepta Therapeutics announced the ...
A former Sussex Police officer has been charged with three offences involving indecent images of a child. George Voisey, 23, was arrested on October 24 and following an investigation has been ...
A sex offender has been jailed after he was found in possession of child sexual abuse images. Lucas Banton, now aged 23, was exposed when an email address linked to him was used to upload two indecent ...
An “experienced and fully-fledged” sex offender with an interest in children coerced a boy and a girl to send him intimate pictures of themselves. In return, Andrew Weir, who had amassed a ...
Lucas Banton was found to have nearly 17,000 indecent images, more than 200 of which were graded as Category A. A man found with 17,000 indecent images of children has been jailed. Lucas Banton ...
The company offers Translarna and Emflaza for the treatment of Duchenne muscular dystrophy; Upstaza to treat aromatic l-amino acid decarboxylas (AADC) deficiency, a central nervous system disorder ...
The fundraiser is inspired, in part, by Michael Kuchwara, a famed Associated Press theater critic who died from pulmonary fibrosis in 2010 Broadway starts are scheduled to perform popular show tunes ...
Newborns in Minnesota can now be screened for Duchenne muscular dystrophy (DMD ... Symptoms usually begin before the child's first birthday but can start as late as 3 years old.
Born with Duchenne muscular dystrophy, Norwegian Mats Steen lived ... Latasha’s friends and family privately mourned the loss of a vibrant child whose full story was never in the headlines.
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