After Sarepta reported the death of a patient who had recently taken the gene therapy Elevidys, patient advocacy group Parent ...

Sarepta Therapeutics said that a young man died after receiving Elevidys, its gene therapy for Duchenne muscular dystrophy ...

A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...

A 12-year-old boy with a severe form of muscular dystrophy ... Duchenne UK, said: "It's just hard to understand with a disease that is so cruel and progressive, and time is muscle, why children ...

Parents see symptoms much earlier and some symptoms are already visible when the children are very young. Duchenne Muscular Dystrophy is named after Dr Duchenne de Boulogne, who was one of the ...

Duchenne muscular dystrophy (DMD) is a genetic condition ... Each time a person who is a carrier of DMD has a child who is assigned male at birth, the child has a 50% chance of developing DMD.