Solid Biosciences advances gene therapies for muscular and cardiac diseases, gaining FDA clearance for SGT-212 and targeting ...
Researchers at the Experimental and Clinical Research Center (ECRC), a joint institution of the Max Delbrück Center and ...
In Benjamin Ree's documentary, Steen's parents learn about their son's rich social life as an avid 'World of Warcraft' gamer ...
RBC Capital notes that Dyne Therapeutics (DYN) announced new clinical data from its ongoing Phase 1/2 ACHIEVE trial of DYNE-101 in patients ...
European regulators are to review Sarepta Therapeutics’ Duchenne muscular dystrophy drug, eteplirsen – a drug that has sparked controversy in the US, where it was approved by the FDA against ...
Seven-year-old Archie Ennis has been diagnosed with Duchenne muscular dystrophy, a genetic condition that causes muscle ...
BACKGROUND Respiratory failure is the commonest cause of death in patients with Duchenne muscular dystrophy (DMD). Life expectancy is less than one year once diurnal hypercapnia develops. This study ...
Minor muscle spasming can occur due to health conditions like nutrient deficiencies. More severe twitching can be a symptom of serious health conditions, including those affecting the nervous ...
45.1 x 31.8 cm. (17.8 x 12.5 in.) ...
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