inews.co.uk on MSN4d
The 3.5m people with rare diseases who face worsening treatment and diagnosis rates
Rare diseases affect one in 17 people in the UK, but a Government initiative designed to improve their quality of life will ...
Stockhead on MSN3d
Crucible: This rare blood disease tackler plans to hit investors with its best shot
The myelofibrosis drug landscape has become more crowded since Syntara decided to focus on the disease in 2020, but the ...
Express Healthcare3d
Rare disease treatment: Look at emerging therapies and medications
Dr Anup Rawool, Consultant in Clinical and Cancer Genetics at Sahyadri Hospitals, Pune, discusses innovative therapies and ...
American Council on Science and Health6d
“Rare” but Not Uncommon: The Hidden Crisis of Rare Diseases
Rare diseases - a medical condition so obscure that even your doctor has to Google. Despite their name, these diseases ...
Experimental treatment borrowed from blood cancer shows promise for pediatric brain tumors
In an early-stage clinical trial, the therapy nearly doubled the expected survival time of young patients. Still, experts ...
Dr Boreham’s Crucible: This rare blood disease tackler aims to hit investors with its best shot
While the myelofibrosis drug landscape has become more crowded since Syntara (then Pharmaxis) decided to focus on that ...
Scottish teenager's double vision led to extremely rare brain tumour diagnosis
Joscelyne Kerr, 19, was diagnosed with an extremely rare brain tumour in 2023 and has been given a prognosis of 12-18 months ...
Derbyshire NHS failed to tell parents about babies' sickle cell risk for 11 years
More than 800 families were not told about their baby’s sickle cell carrier status, identified through a heel prick blood ...
Mirage News1d
FDA OKs Drug for Rare Genetic Disorder, Offers Hope
OHSU's pioneering research, clinical trials led to better testing, approval for CTX disease Eric Stewart has a rare disease ...
Teenager diagnosed with extremely rare brain tumour aftter noticing double vision
Initially, an optician in June of that year suspected it to be a rare neurological condition known as Adie pupil. However, as ...
The Truth About Alzheimer’s Disease and Genes
Here, experts explain genetics in Alzheimer’s and dementia, including if it’s hereditary, how to lower your risk, and ...