inews.co.uk on MSN4d
The 3.5m people with rare diseases who face worsening treatment and diagnosis rates
Rare diseases affect one in 17 people in the UK, but a Government initiative designed to improve their quality of life will ...
Fierce Pharma13d
With blood and growth disorder bids panning out, Novo Nordisk plots path to rare disease leadership: exec
Still, Novo is steadfast in its goal to eventually become a leader in the space, the company’s EVP of rare disease, Ludovic ...
Stockhead on MSN3d
Crucible: This rare blood disease tackler plans to hit investors with its best shot
The myelofibrosis drug landscape has become more crowded since Syntara decided to focus on the disease in 2020, but the ...
Express Healthcare3d
Rare disease treatment: Look at emerging therapies and medications
Dr Anup Rawool, Consultant in Clinical and Cancer Genetics at Sahyadri Hospitals, Pune, discusses innovative therapies and ...
American Council on Science and Health6d
“Rare” but Not Uncommon: The Hidden Crisis of Rare Diseases
Rare diseases - a medical condition so obscure that even your doctor has to Google. Despite their name, these diseases ...
Dr Boreham’s Crucible: This rare blood disease tackler aims to hit investors with its best shot
While the myelofibrosis drug landscape has become more crowded since Syntara (then Pharmaxis) decided to focus on that ...
Experimental treatment borrowed from blood cancer shows promise for pediatric brain tumors
In an early-stage clinical trial, the therapy nearly doubled the expected survival time of young patients. Still, experts ...
What is Alzheimer's disease and how is it detected?
"Alzheimer's disease is a brain disorder that slowly destroys memory and thinking skills and, eventually, the ability to ...
This internationally recognized NJ doctor is on the frontlines battling rare diseases
A rare disease in the US is one in 1,500, or fewer than 200,000 people, and an ultra-rare disease is one in 50,000 or fewer than than 6,000 people.
Fierce Biotech8d
Ono pays $280M upfront for Ionis' antisense oligonucleotide for rare blood cancer
Japan's Ono Pharmaceutical is handing over $280 million upfront to acquire Ionis Pharmaceuticals’ phase 2-stage antisense ...
Warwick 'lights it up' to surprise 6-year-old with rare disease
Many have heard about "Good Night Lights" for patients at Hasbro Children's Hospital, and recently, a Warwick boy was the recipient of something similar.
Gene Hackman Died Of Heart Disease—And Wife Killed By Rare Mouse-Borne Virus, Officials Say
Gene Hackman, 95, and Betsy Arakawa, 65, were found dead in their home on Feb. 27 of natural causes, New Mexico officials ...