Thomas E. Fischer, diagnosed with Inclusion Body Myositis, gradually lost his ability to walk, and lost much of the strength in his hands, but spends time focusing on his "wonderful wife, four ...

The study looked at people with a variety of neuromuscular diseases that cause muscle weakness and loss, including muscular dystrophies; post-polio syndrome, a condition that appears decades after ...

Argenx reports long-term Vyvgart data showing lasting efficacy in gMG and CIDP, with strong safety and symptom control across multiple studies.

Aarhus, Denmark, 25 March 2025 - NMD Pharma A/S, a clinical-stage biotech company dedicated to developing novel and improved treatments for patients living with neuromuscular diseases, today announces ...

Session ID: 2025-06-29:2924e2abda97a390b2ca2482 Player Element ID: vjs_video_3 ...

Califf, now an instructor of medicine at Duke University, did not shy away from calling out the trends he sees as threats to care delivery and research: The US has a “uniquely inadequate ...

A UConn professor and researcher who 28 years ago discovered a gene for a protein that limits human muscle growth is closer than ever to having that work play a significant role in treating those ...

In recognition of Rare Disease Day, Avidity is supporting a range of activities in efforts to build broader awareness of rare diseases including DMD, DM1 and FSHD, such as: ...

Report with the AI impact on market trends - The global neuromuscular disease therapeutics market size is estimated to grow by USD 13.73 billion from 2025-2029, according to Technavio. The market ...

BRISBANE, Calif., Nov. 25, 2024 /PRNewswire/ -- ReviR Therapeutics, a pioneering biotechnology company focused on developing novel small molecule RNA modulators for neurogenetic diseases ...