Orchard Therapeutics Announces Multiple Data Presentations and Receives 2025 New Treatment Award at the 21st Annual WORLDSymposium™
Featured data showcase the transformative potential of HSC gene therapy to enable cross-correction and restore enzymatic ...
BioSpace21hOpinion
Opinion: Companies Vie to Develop a Hunter Syndrome Therapy That Reaches the Brain
Several companies—including JCR Pharmaceuticals, Denali Therapeutics and Regenxbio— have products in the pipeline that could ...
Gene therapy may be 'one-shot stop' for rare bone disease
For the last 10 years, the only effective treatment for hypophosphatasia (HPP) has been an enzyme replacement therapy that ...
Microscopy approach offers new way to study cancer therapeutics at single-cell level
Understanding how tumors change their metabolism to resist treatments is a growing focus in cancer research. As cancer cells adapt to therapies, their metabolism often shifts, which can help them ...
Healio21h
VIDEO: Treatment flow employed for EGFR-mutated lung cancer
In this video, Xiuning Le, MD, PhD, discusses how she approaches putting together a treatment plan for a patient with EGFR-mutated lung cancer.
Healio21h
VIDEO: Treatment options limited after EGFR-mutated lung cancer relapse
In this video, Xiuning Le, MD, PhD, discusses the greatest areas of unmet need in the treatment of EGFR-mutated lung cancer.