Discover Sanfilippo Syndrome a rare genetic disorder affecting childrens development Learn about its symptoms treatment ...
GlobalData on MSN11d
Regenxbio and Nippon Shinyaku forge $810m gene therapy dealRegenxbio will receive $110m upfront from Nippon Shinyaku and is eligible to get up to $700m in development, regulatory, and ...
Mucopolysaccharidosis (MPS ... We report the allele frequency of common mutations for each gene in our patient cohort and the exonic distribution of coding sequence alterations in the IDS ...
The US gene therapy company Regenxbio and the Japanese firm Nippon Shinyaku have joined forces to boost the development and ...
Denali’s candidate is its DNL12 enzyme replacement therapy (ERT) for mucopolysaccharidosis ... Neurogene has contributed its gene therapy NGN-401 for Rett syndrome, a rare genetic neurological ...
As the year unfolds the biotech industry will look closely at these ten first-in-class drugs on track to reach FDA approval ...
Scientists at the Broad Institute of MIT and Harvard, Harvard Medical School, and McLean Hospital have discovered a ...
Researchers have discovered a biological mechanism that makes plant roots more welcoming to beneficial soil microbes. This ...
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