Hunter syndrome affects over 2,000 individuals ... demonstrating positive effects on evidence-based surrogate endpoints and early signs of improved clinical outcomes. Denali's Chief Medical (TASE:PMCN ...

The macaques exposed via the mouth or stomach, however, had limited infection but showed no signs of illness. All the monkeys ...

With an FDA approval submission for RegenXBio’s Hunter syndrome gene therapy already underway, the biopharma has now found a commercialization partner for both the U.S. and Asian markets.

Hunter syndrome results from the absence of an enzyme needed to break down cellular waste. Without it, waste builds up in the body, causing progressive damage to various systems.

with positive effects on evidence-based surrogate endpoints and early signs of improved clinical outcomes in participants with Hunter syndrome. This designation will provide Denali with more ...

"[T]he arrival on the US political scene of emails purportedly belonging to Vice President Biden's son Hunter, much of it related to his time serving on the Board of the Ukrainian gas company ...

Denali Therapeutics Inc. DNLI announced that the FDA has granted Breakthrough Therapy Designation to its pipeline candidate, tividenofusp alfa (DNL310), for the treatment of individuals with Hunter ...

New buses with seatbelts will need to have signs and audio announcements reminding ... are in response to the 2023 Hunter Valley bus crash. Rules to be introduced over the next few years will ...