theAsianparent on MSN9d
Getting to Know Waardenburg Syndrome, a Rare and Miraculous Genetic Disorder
It could be that this magical condition is known by the medical term Waardenburg syndrome. Waardenburg syndrome affects about ...
CBS News13d
Mystery disease in Congo may be from poisoned water source, WHO says. Here's what to know.
How many deaths have been linked to the mystery disease in Congo? At least 60 deaths have been reported, according to the latest bulletin from the WHO's Africa office. In the initial outbreak ...
Healthline14d
How Does Crohn’s Disease Affect Your Poop and Bowel Movements?
Crohn’s disease is an inflammatory bowel disease (IBD) that can lead to blood in bowel movements. It can also change the frequency and color of poop. Medications, diets, and lifestyle changes ...
verywellhealth15d
Peripheral Artery Disease and How It's Treated
Peripheral artery disease (PAD) is a condition in which one or more of the arteries supplying blood to the body, flowing away from the heart, become blocked or partially blocked. This often reduces ...
BioWorld16d
Neurenati’s NEU-001 awarded orphan drug designation for Hirschsprung disease
Neurenati Therapeutics Inc.’s NEU-001 has been awarded U.S. orphan drug and rare pediatric disease designations by the FDA for the treatment of Hirschsprung disease.
BioSpace16d
The US FDA Grants Both Orphan Drug and Rare Pediatric Disease Designations to NEU-001 of Neurenati for the Treatment of Hirschsprung Disease
Neurenati Therapeutics is a Québec-based biotech company dedicated to developing innovative therapies for rare diseases. Its lead program focuses on Hirschsprung disease (HD), a life-threatening ...
Medical Xpress16d
How to clear the toxic tau protein that can lead to Alzheimer's and related diseases
The scientists produced these organoids from stem cells derived from healthy people as well as from patients with neurodegenerative diseases related to tau toxicity. When exposed to glutamate ...
Columbus Dispatch16d
Columbus native who won MrBeast's 'Beast Games' rucks across California on behalf of son
The goal of his journey, titled "Ruck 4 Rare", is to raise awareness of Lucas' disease and other creatine disorders, raise money for treatments and a cure, and to show other families suffering ...
ABC News16d
CDC says it is monitoring mysterious deadly disease in Congo
At least 1,318 people have exhibited symptoms and 53 have died, the WHO said. The U.S. Centers for Disease Control and Prevention is closely monitoring an unknown disease that has killed dozens in ...
Business Wire17d
The US FDA Grants Both Orphan Drug and Rare Pediatric Disease Designations to NEU-001 of Neurenati for the Treatment of Hirschsprung Disease
ABOUT NEURENATI Neurenati Therapeutics is a Québec-based biotech company dedicated to developing innovative therapies for rare diseases. Its lead program focuses on Hirschsprung disease (HD), a ...
Yahoo Finance17d
The US FDA Grants Both Orphan Drug and Rare Pediatric Disease Designations to NEU-001 of Neurenati for the Treatment of Hirschsprung Disease
and Rare Pediatric Disease Designation (RPDD) to NEU-001, a novel combination therapy utilizing a neurotrophic growth factor, for the treatment of Hirschsprung disease (HD). NEU-001 is a first-in ...