Despite having gone through this before with her first son, Yusof, and despite the doctors explaining that this was a gene ...

Hunter syndrome results from the absence of an enzyme needed to break down cellular waste. Without it, waste builds up in the body, causing progressive damage to various systems.

Haliza Md Kasim’s eyes widened. Despite having gone through this before with her first son, Yusof, and despite the doctors ...

In 2021, the FDA granted Fast Track designation to tividenofusp alfa for the treatment of patients with Hunter syndrome ... mutations confirmed by genetic testing. BIIB122 is also being evaluated ...

Denali obtains Breakthrough Therapy Designation for its experimental candidate, tividenofusp alfa (DNL310), for the treatment of pateints with Hunter syndrome.

The partnership between REGENXBIO and Nippon Shinyaku is more than just a standard collaboration—it’s a bold, forward-looking venture aimed at bringing revolutionary gene therapies to market for rare, ...

DIABETES, Parkinson's disease, degenerative disc disease, macular degeneration, stroke — what do these have in common?

Finally, a dancer cried out: "Stop the music!" A group of people rushed to the stage. Someone recognized that Hunter's heart ...