What is Cushing's syndrome? Cushing's syndrome is a hormonal disorder. It’s caused when you have high levels of the hormone cortisol over a long time. Cushing's syndrome is fairly rare. It most often ...

A North Georgia teen is beating the odds. He survived a rare syndrome that took place in his mother's womb. The amniotic sac tears and sometimes strangles the unborn child.

Despite having gone through this before with her first son, Yusof, and despite the doctors explaining that this was a gene ...

Haliza Md Kasim’s eyes widened. Despite having gone through this before with her first son, Yusof, and despite the doctors ...

A man was diagnosed with skeletal fluorosis, which likely emerged due to him inhaling substances that damaged his bones.

Gold medal in the grandest track and field sports arena? The post Grateful Paralympic Gold Medalist Hunter Woodhall Recalls ...

The deal with Nippon Shinyaku announced Tuesday will hand over partial responsibility to Regenxbio’s most advanced wholly ...

In 2021, the FDA granted Fast Track designation to tividenofusp alfa for the treatment of patients with Hunter syndrome ... Director of Research Sheraz Mian hand-picks one to have the most ...

Denali’s wholly owned program, DNL310 or tividenofusp alfa, is an Enzyme Transport Vehicle-enabled iduronate-2-sulfatase (IDS) replacement therapy in development for MPS II (Hunter syndrome).

This designation is in addition to Fast Track Designation, Orphan Drug Designation, and Rare Pediatric Disease Designation, all previously granted by the FDA for tividenofusp alfa in Hunter syndrome.

Hunter syndrome affects over 2,000 individuals, primarily males, in commercially accessible regions. With analysts maintaining a Strong Buy consensus and the company maintaining a healthy liquidity ...