US biotech Regenxbio (Nasdaq: RGNX) has successfully completed the BLA submission for its mucopolysaccharidosis II (MPS II) ...

Regenxbio closes strategic partnership with Nippon Shinyaku for MPS diseases: Rockville, Maryland Wednesday, March 5, 2025, 14:00 Hrs [IST] Regenxbio Inc., a leading clinical-stag ...

REGENXBIO Inc.  today announced the closing of its previously announced strategic partnership with Nippon Shinyaku. Under the terms of the agreement, REGENXBIO and Nippon Shinyaku will develop and ...

Regenxbio (RGNX) announced the closing of its previously announced strategic partnership with Nippon Shinyaku. Under the terms of the ...

More info Erica Boyce, a Dublin mum, is at her wit's end as the State's failure to find a school place for her autistic Down's Syndrome son Marley is wreaking havoc on her mental health.

The Island’s two MPs were at odds over a motion defending County Hall’s independence at a crucial full council meeting on Wednesday evening. Isle of Wight West MP Richard Quigley (Labour ...

Parents are expressing concerns about a lack of communication from MPS regarding lead remediation efforts. Lead-Safe Schools MKE is advocating for stricter testing protocols and a focus on ...

Jesus Luzardo was dominant on the mound in the Philadelphia Phillies’ 7-5 win over the Boston Red Sox on Friday. Per MLB.com’s Todd Zolecki, Luzardo stifled the Red Sox in his first taste of Spring ...

For example, Cord Blood Stem Cell Transplants are one time curative treatment for many rare diseases such as Inborn Errors of Metabolism (Lysosomal Storage Disorders (LSDs), Mucopolysaccharoidosis ...

Government sources say they are preparing for challenging conversations about the proposed changes – knowing that any suggestion of restricting benefits will be unpopular among Labour MPs.