MIRM's high reliance on lead drug, Livmarli for revenues remains a worry. Failure to generate sufficient revenues from Livmarli sales is likely to hurt the stock.

What is Guillain-Barré syndrome? Guillain-Barré syndrome (GBS) is also called acute inflammatory demyelinating polyradiculoneuropathy (AIDP). It's a neurological disorder in which the body's immune ...

Indian teen Lalit Patidar has set a Guinness World Record for the hairiest face, with 201.72 hairs per square centimeter, due to a condition called hypertrichosis. Despite early challenges and ...

Down Syndrome Ireland’s Donegal branch is gearing up for World Down Syndrome Day on Friday 21st of March. Ahead of the big day, the branch is shining a spotlight on one of their wonderful members Seán ...

Superior vena cava (SVC) syndrome is a set of symptoms that occur when blood flow through the superior vena cava is partially or fully blocked. The superior vena cava is the large blood vessel that ...

From reproductive rights to climate change to Big Tech, The Independent is on the ground when the story is developing. Whether it's investigating the financials of Elon Musk's pro-Trump PAC or ...

However, the association between metabolic syndrome (MetS) and early-onset CRC remains unexamined. Design We conducted a nested case–control study among participants aged 18–64 in the IBM MarketScan ...

Thus, Gilles de la Tourette's disease is not the same as what today is labeled Tourette syndrome. Outside Charcot's circle, most physicians believed that multiple motor tics and coprolalia were a ...

12 14 23 27 Only short stature was significantly associated with molecular diagnoses, reflecting diagnoses of Noonan, Kabuki, Alagille and CHARGE syndrome as well as rarer single-gene disorders, such ...

LIVMARLI's net product sales increased by 50% compared to 2023, driven by strong demand in Alagille syndrome and PFIC. The FDA approved CTEXLI for cerebrotendinous xanthomatosis (CTX) in adults ...

LIVMARLI® (maralixibat) oral solution is an orally ... It is approved for the treatment of cholestatic pruritus in patients with Alagille syndrome (ALGS) in the U.S. three months of age and ...