News

Scarlett's Mini Golf Gala benefits Woodbridge child with rare genetic disorder
WOODBRIDGE – A fundraiser to benefit brave 4-year-old township resident Scarlett Griffith and heighten awareness about the ...
Boston Marathon runner carries memory of 5-year-old patient with her on race day
Gio passed away a couple of years ago from a rare genetic condition called Morquio A syndrome. He spent quite a few months at ...
Boston Marathon runner carries memory of 5-year-old Biddeford boy across the finish line
Monday marks the 129th Boston Marathon, with more than 200 Mainers among the 30,000-plus runners in the field.However, not ...
pharmaphorum3y
NICE firms up NHS use of Vimizim for Morquio A syndrome
In 2015, NICE said that BioMarin's Vimizim could be used to treat patients with the ultra-rare disease Morquio A syndrome, while real-world data was collected on its efficacy. Now – almost seven ...
MyCentralJersey6d
Scarlett's Mini Golf Gala benefits Woodbridge child with rare genetic disorder
All proceeds from Scarlett’s Mini Golf Gala will directly support Scarlett’s ongoing medical care and research toward developing a cure for Morquio A Syndrome, which affects just four in 1 ...