Duchenne muscular dystrophy's impact on the brain may be reversible
New research led by the University of Portsmouth has revealed how Duchenne muscular dystrophy (DMD), best known for causing ...
The American Journal of Managed Care19h
WVE-N531 Shows Functional Benefits, Muscle Damage Reversal in DMD
WVE-N531 demonstrated statistically significant improvements in muscle biopsy measures and functional measures in patients ...
The American Journal of Managed Care1d
Real-World Study Suggests DMD Gene Therapy Is Safe, Effective
Delandistrogene moxeparvovec, a gene therapy approved for the treatment of Duchenne muscular dystrophy (DMD), was found ...
Wave Life Sciences to submit Duchenne drug for approval after Phase 2 success
The Cambridge-based biotech's experimental treatment for Duchenne muscular dystrophy hit the mark in a mid-stage study, ...
STAT2d
Wave to submit Duchenne drug for approval after Phase 2 success
Wave Life Sciences’ experimental treatment for Duchenne muscular dystrophy hit the mark in a mid-stage study, setting the ...
SMA News Today3d
MDA 2025: Potassium channel could be SMA treatment target
Activating a protein called potassium channel Kv2.1 may help improve motor function in SMA, making it a potential SMA ...
SMA News Today3d
MDA 2025: Potassium channel seen potential SMA treatment target
Activating a protein called potassium channel Kv2.1 may help improve motor function in SMA, making it a potential SMA ...
Science Daily3d
Target to repair injured muscles discovered
A team has discovered a possible therapeutic approach to repair injured muscles either from aging or degenerative muscle disorders.