Researchers have discovered a potential therapeutic target in muscular disorders by identifying a previously unrecognized ...

A team has discovered a possible therapeutic approach to repair injured muscles either from aging or degenerative muscle disorders.

Amid readouts from the Muscular Dystrophy Association’s annual meeting, the Clinical Trials Arena evaluates five DMD trials ...

An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

As it gears up to submit an approval application next year, Wave Life Sciences has presented fresh phase 2 data showing its ...

For millions of people, losing muscle isn't just about weakness; it's about losing independence. Whether caused by Duchenne muscular dystrophy, aging or other degenerative conditions, muscle loss can ...

Avidity Biosciences Inc. says will submit an application for accelerated approval to the FDA for del-zota before the end of ...

For millions of people, losing muscle isn't just about weakness; it's about losing independence. Whether caused by Duchenne muscular dystrophy, aging ...

Giulio Cossu, MD, speaks to the lingering safety concerns related to ex vivo gene therapy in Duchenne muscular dystrophy (DMD) as long-term data are yet to be established.

Precision BioSciences (DTIL) announced the presentation of preclinical data for its PBGENE-DMD development program for the treatment of ...

Colton Belluzzo was diagnosed with a form of muscular dystrophy when he was a baby ... “This spreads around and gets into the muscle cells,” said Karachunski. The virus isn’t harmful ...