FDA Grants Orphan Drug Designation to IPS HEART’s GIVI-MPC Stem Cell Therapy for Becker Muscular Dystrophy
IPS HEART has been awarded Orphan Drug Designation (ODD) by the FDA for GIVI-MPCs based on its unique ability to create new ...
Struggling With Muscle Weakness? It May Be A Sign Of Muscular Dystrophy
Muscular Dystrophy (MD) is a genetic condition causing progressive muscle weakness and complications in vital organs. Early ...
Medical Xpress19d
CRISPR therapy corrects muscular dystrophy mutations and regrows muscles in mice
The dysferlin protein is primarily responsible for repairing cell membranes. People with certain mutations in the gene coding for dysferlin develop muscular dystrophy—a group of muscle wasting ...
technologynetworks18d
CRISPR Therapy Shows Promise for Muscular Dystrophy in Mice
The dysferlin protein is primarily responsible for repairing cell membranes. People with certain mutations in the gene coding for dysferlin develop muscular dystrophy – a group of muscle wasting ...
Business Wire13d
FDA Grants Orphan Drug Designation to IPS HEART’s GIVI-MPC Stem Cell Therapy for Becker Muscular Dystrophy
IPS HEART has now shown GIVI-MPCs create new human muscle with full length human dystrophin in dystrophic pigs, young and extremely aged Duchenne Muscular Dystrophy (DMD) mice and in a sarcopenia ...
Power loading: a drug for rare forms of muscular dystrophy has been tested in the Russian Federation
According to the scientists of the National Research University "BelSU", the obtained results allow us to conclude that the ...
EurekAlert!19d
Developing a CRISPR therapy for muscular dystrophy
The dysferlin protein is primarily responsible for repairing cell membranes. People with certain mutations in the gene coding for dysferlin develop muscular dystrophy – a group of muscle wasting ...