Despite the obstacles, Riley Herrera had a life filled with family, sports, travel, faith and hope before his death on Nov.

Columnist Betty Vertin has learned that as a parent, she's finding the years with all her children, including those with DMD, too short.

A seven-year-old boy from Dublin is on his way to California to undergo testing after being diagnosed with a rare condition ...

While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...

The gene therapy improved motor functions in children with Duchenne muscular dystrophy two years after treatment ...

An investigational higher dose of spinal muscular atrophy drug nusinersen gains attention as the FDA and European Medicines ...

Roche and Sarepta Therapeutics have shared positive top-line results from a late-stage study of Elevidys (delandistrogene ...