Sanofi has added another string to its Pompe disease therapy bow ... the market four years later to treat late-onset Pompe in children aged over eight. In 2010, Lumizyme's label was expanded ...

With the right policies, advanced science, and strong leadership in government agencies, Donald Trump has the power to save ...

we continue to enroll the ongoing open label ZIP study for children living with late-onset Pompe disease and the open label Rossella study for children living with infantile onset Pompe disease.

“Like Gaucher disease, Pompe disease, Fabry disease ... leaving patients, most of whom are children, in dire circumstances. Initial investments in the well-being of patients are wasted if ...

AskBio Inc. (AskBio), a gene therapy company wholly owned and independently operated as a subsidiary of Bayer AG, today announced the advancement of the Phase 1/Phase 2 LION-CS101 clinical trial of ...

Parkinson’s disease, and Pompe disease. AskBio’s gene therapy platform includes Pro10™, an industry-leading proprietary cell line manufacturing process, and an extensive array of capsids and ...

The most elaborate wellness routine won't work if you neglect the basics. Dieticians, personal trainers, GPs, physios and ...

Prince Frederik of Luxembourg died from a genetic disease called PolG, but experts hope his passing could bring more awareness to the rare condition that impacted his life.

After a decade of searching for an answer to what was causing progressive pain and weakness in my body, I was finally diagnosed with Pompe disease. Pompe, a rare genetic disorder, has long presented a ...