and commercialization of novel products for the treatment of rare and ultra-rare genetic diseases in North America, Latin America, Japan, Europe, and internationally. Its biologic products include ...

Data from the first patients enrolled into Regenxbio's trial of its gene therapy for rare inherited disease mucopolysaccharidosis ... that could correct the genetic defect n MPS I, but that ...

Cats are beloved family members in tens of millions of households, but we know surprisingly little about their genes.

Join the movement to solve the mysteries of cat genetics with the first fur-based DNA sequencing method for pets ...

Most rare diseases, 80% or more, have genetic origins. Some are due to a single defect in a gene with additional mutations in the same gene, resulting in varying severity and presentation. Muscular ...

Scientists say a concerning genetic mutation has appeared in H5N1 bird flu infected cats living in a New Jersey suburb of New ...

Blossom has gone from being 'completely paralysed' to walking up to her owner to greet her thanks to the public donating to ...

The study of rare diseases has already provided fundamental understandings of genetic systems, biochemical pathways, and DNA-repair mechanisms that have helped elucidate the basis of and improve ...

An H5N1 bird flu mutation associated with increased infectiousness and disease severity has been found in two cats. Since the beginning of this year, more than 50 cats have been infected with H5N1 ...

However, a growing number of studies have suggested that kids growing up in a home with "furred animals" -- whether it's a pet cat or dog ... the red flag for heart disease, says Justice.