An ad hoc committee of the National Academies of Sciences, Engineering, and Medicine will develop a strategic plan and blueprint for addressing thalassemia in the United States. In conducting its work ...

Opens in a new tab or window Share on LinkedIn. Opens in a new tab or window An essential factor in distinguishing thalassemia phenotypes is transfusion dependence. While beta-thalassemia major ...

Beta thalassemia is an inherited blood disorder in which the body doesn't make as much beta globin as it should. Beta globin and alpha globin are building blocks of hemoglobin. Hemoglobin is the part ...

Alpha thalassemia is an inherited blood disorder in which the body doesn't make as much alpha globin. Alpha globin is a building block of hemoglobin. Hemoglobin is the part of red blood cell (RBC) ...

Severe alpha thalassemia may lead to fetal demise or a life-long need for chronic transfusions with multiple medical complications, especially iron overload from transfusions. Develop lentiviral ...