A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...
In terms of response, it met its primary end point in all 3 doses. 1 The ORR was 50% or higher [in all 3 groups]. The dose of ...
Sarepta Therapeutics said Tuesday that a patient died while taking its closely watched gene therapy for muscular dystrophy, ...
The Black Wall Street Times on MSN1h
Sickle cell treatment that "cured" New York patient costs millionsSebastien Beauzile’s recently announced cure from sickle cell disease brings hope to thousands of mostly Black Americans who ...
The patient, whom Sarepta described as a young man and later told news outlets was 16 years old, suffered acute liver failure ...
Cambridge-based Sarepta Therapeutics said Tuesday that a patient died while taking its closely watched gene therapy for ...
Every morning at kindergarten, Sarah's middle child ran straight to the dress-up box and put on the brightest pink dress with ...
Titled “State of the Industry—The Evolving Landscape of Healthcare Coverage and Access in 2025,” 1 the goal of the Access USA ...
A new research paper was published by Aging (Aging-US) on March 7, 2025, titled "Accelerated aging associated with cancer characteristics and treatments among breast cancer survivors." ...
Leaders with Lutheran Health Network (LHN) introduced a sweet new staff member on Tuesday—a therapy dog named Pepper.
An Ohio court has overturned part of the state’s law banning certain healthcare for transgender youth, allowing patients to again receive prescriptions like ...
Elevidys was approved after intense debate at the FDA, as officials and reviewers disagreed over how strong the evidence was ...
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