WVE-N531 demonstrated statistically significant improvements in muscle biopsy measures and functional measures in patients ...

For millions of people, losing muscle isn't just about weakness; it's about losing independence. Whether caused by Duchenne muscular dystrophy, aging or other degenerative conditions, muscle loss can ...

Delandistrogene moxeparvovec, a gene therapy approved for the treatment of Duchenne muscular dystrophy (DMD), was found ...

Researchers focused on Myotonic Dystrophy 1 heart problems are testing a novel approach to restore normal function.

An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

RGX-202, a DMD gene therapy, has been well tolerated in an ongoing clinical trial and improved motor function for DMD boys, ...

ROCKVILLE, MD, USA I March 19, 2025 I REGENXBIO Inc. (Nasdaq: RGNX) today reported new, positive interim data from two additional patients in the Phase ...

Sarepta Therapeutics (SRPT) stock drops 25% as the company reports a patient death linked to Elevidys, its gene therapy developed with Roche (RHHBY). Read more here.

More than 150,000 people are affected by muscular dystrophy in the UK - 30,000 suffer directly as a result of their condition but a further 120,000 people including families and carers have had ...

It also stretches to help open and close the urethra during urination (peeing). The vagina is a muscular tube that provides the passageway from the outside of the body to the uterus (womb). It changes ...

For the fourth consecutive year, Han-Dee Hugo’s, 1190 Long Ferry Road, Salisbury will be hosting a MDA Festival to raise ...

There are five types of SMA relating to age of onset and symptom severity. Muscular dystrophy is a group of progressive conditions that cause loss of muscle mass and weakness. It occurs when one ...