Treatment focuses on symptom management and is carried out by a multidisciplinary team. Currently, miglustat, (Zavesca™; Actelion Pharmaceuticals Ltd), inhibitor of the synthesis of GSLs is the first ...

Faculty of Pharmaceutical Sciences, Hokuriku University, Ho-3 Kanagawa-machi, Kanazawa 920-1181, Japan, Department of Pharmaceutical Botany, Faculty of Pharmacy, Mahidol University, Thailand, The Food ...