News

Biogen raises annual profit forecast on strong demand for rare disease drugs
Biogen raised its annual profit forecast and beat estimates for quarterly results on Thursday, as strong demand for its rare ...
Biogen Lifts Outlook As Rare Disease And Alzheimer's Drug Sales Accelerate
Biogen Inc. (NASDAQ:BIIB) reported on Thursday that the second quarter of 2025 adjusted earnings per share were $5.47, up 4% ...
Medical Marketing & Media1d
Rare disease patients, caregivers are at odds over health information
The survey primarily focused on rare disease patients between the ages of 16 and 23, as well as caregivers between 25 to 55 years old. Hemophilia, albinism, cystic fibrosis and Gaucher disease were ...
GeneDx CEO on rare disease diagnosis: Earlier testing gives families and clinicians more options
Katherine Stueland, GeneDx CEO, joins 'Squawk Box' to discuss diagnosing children with rare diseases, cost structure of the ...
Rare Disease Drugmakers Shift Plans After Win in Trump Megabill
The pharmaceutical industry has a fresh sense of direction after President Donald Trump’s tax-and-spending law included a ...
Rare tick-borne virus causing neurological symptoms diagnosed in Northeastern state
Rare Powassan virus case in Maine highlights serious tick-borne illness with no vaccine or treatment, causing neurological symptoms and potential fatality.
Neurology Advisor8d
Child’s Rare Neurodegenerative Disease Fuels Therapy Innovation: Paxton’s Story
The Purdy family shares their insights on navigating their child’s rare neurodegenerative disease and their direct ...
Research Moves Slowly. Rare Diseases Don't—So Patients Aren't Waiting
Patients with rare diseases are increasingly working to find and fund their own cures. But should they have to?
Nanaimo News Bulletin13h
Conservative health critic says B.C. falls short on rare disease drug coverage and transparency
In a video posted to her Facebook page, the Conservative health critic said she was shocked to learn how badly B.C. ranks ...
EARLY YEARS: Virginia teen with rare disease launches nonprofit to encourage youth to advocate for their heath
Rising high school senior Khartik Uppalapati says he felt alienated when he was diagnosed with a rare lymphatic disorder ...
Norfolk Daily News16h
Nebraska family finds strength in community while fighting rare disease
Originally from Bow Valley and Hartington, Terry and Stacy Thoene raised Ollie in Lincoln before building a house in Eagle in 2021. Their parish, friends and neighbors have stepped up with ...