News

The U.S. Food and Drug Administration has approved Empaveli (pegcetacoplan) as the first treatment for C3 glomerulopathy (C3G ...
Daniel Cressy will be the first patient in Louisiana to complete the gene therapy treatment for sickle cell disease.
The primary safety risks associated with gene therapy include immune reactions and off-target effects in unintended organs, such as the liver, lungs, and spleen. Nevertheless, Ali and Townsend note ...
Chris Kirkpatrick is in awe that his former ‘NSync bandmate Justin Timberlake performed a full tour amid a battle with Lyme ...
Dr. Michael Wagner covers the basics of epithelioid hemangioendothelioma, a rare vascular cancer, spanning symptoms, ...
A stellar launch of the rare heart disease med Amvuttra has boosted Alnylam’s market cap above $50 billion. | A stellar launch of Amvuttra in the rare heart disease ATTR-CM has boosted Alnylam’s ...
Sanofi is handing over $130 million upfront for the China rights to Arrowhead Pharmaceuticals’ rare metabolic disease ...
Apellis Pharmaceuticals Inc. (NASDAQ:APLS) is one of the biotech stocks to buy according to Wall Street analysts.
CM, Kawasaki Disease, Chagas Disease, and Rheumatic Heart Disease are becoming increasingly recognized, though often ...
SAR446523, an investigational antibody targeting GPRC5D, received FDA orphan drug status and is in phase 1 trials for ...
Biogen Inc. (NASDAQ:BIIB) reported on Thursday that the second quarter of 2025 adjusted earnings per share were $5.47, up 4% ...
Chris Kirkpatrick is praising Justin Timberlake for pushing through his tour while battling Lyme disease. On July 31, ...