Shirley MacFarland’s weekly community column featuring news and notes from Brecksville, Broadview Heights, North Royalton and ...

U.S. Sen. Richard Blumenthal and researchers raise the alarm on how a federal medical research funding cap could impact "life ...

Thinking her little boy had trouble with balance when he started to have minor falls Kelly took William to see a pediatrician ...

After Sarepta reported the death of a patient who had recently taken the gene therapy Elevydis, patient advocacy group Parent ...

RGX-202, a DMD gene therapy, has been well tolerated in an ongoing clinical trial and improved motor function for DMD boys, ...

The interim data found one child in the Duchenne trial produced more than double the amount of the protein needed to maintain ...

Cumberland Pharmaceuticals Inc. , a specialty pharmaceutical company with development efforts focused on rare diseases, today announced that results from its Phase 2 FIGHT DMD clinical trial were ...

Avidity Biosciences Inc. says will submit an application for accelerated approval to the FDA for del-zota before the end of ...

Cargo was founded by two highly acclaimed cell-therapy researchers. The company raised over $500 million to develop ...

REGENXBIO Inc. (Nasdaq: RGNX) today reported new, positive interim data from two additional patients in the Phase I/II portion of the AFFINITY DUCHENNE® trial of RGX-202, a differentiated ...

Amplify LatinX has rebranded as We Are ALX Inc. and added three new board members: Cynthia Izzo, principal at KPMG US; Melissa Luna, executive director of GreenLight Boston; and Francisco Marriott, VP ...

Wheelchairs 4 Kids and Rooms To Go Furniture partnered to give one Yankees fan a chance to throw out the first pitch of the Yankees spring training game against the Red Sox at Steinbrenner Field.