McGill University Health Centre5d
Major funding for research project on cystic fibrosis
A new research project focusing on rare genetic mutations that are linked to cystic fibrosis just received $600,000 in ...
The Pharma Letter12d
MHRA backing for Alyftrek for cystic fibrosis
The UK’s Medicines and Healthcare products Regulatory Agency (MHRA) has today approved Alyftrek (triple combination medicine ...
Pharmabiz10d
UK MHRA approves Vertex’s Alyftrek, a once-daily next-in-class CFTR modulator to treat cystic fibrosis
UK MHRA approves Vertex’s Alyftrek, a once-daily next-in-class CFTR modulator to treat cystic fibrosis: London Monday, March 10, 2025, 10:00 Hrs [IST] Vertex Pharmaceuticals, a ...
Mirage News12d
Triple Combo Drug Approved for Cystic Fibrosis
In two randomised phase 3 studies involving 480 participants aged 12 years and over, ivacaftor/tezacaftor/vanzacaftor was ...
Where Will Vertex Pharmaceuticals Be in 10 Years?
The past decade has been a game-changing one for Vertex Pharmaceuticals (NASDAQ: VRTX). The biotech won approval for its ...
Medindia24d
Inhalable Gene Therapy Trialed for Cystic Fibrosis Patients
Cystic fibrosis is an inherited lifelong disease that gets worse over time. It is estimated to affect 105,000 people worldwide. There are more than 2,000 known mutations in the CFTR gene ...
Medical Xpress28d
Novel inhalable gene therapy trialed for people with cystic fibrosis
Cystic fibrosis is an inherited lifelong disease that gets worse over time. It is estimated to affect 105,000 people worldwide. There are more than 2,000 known mutations in the CFTR gene ...
Business Wire22d
FDA Grants Orphan Drug Designation to Revolutionary Cystic Fibrosis Therapy
Cystic fibrosis is a genetic disorder that adversely ... accounting for approximately 70% of all CFTR mutations. It is estimated that more than 160,000 people worldwide are living with CF ...
News Medical28d
Inhalable gene therapy tested for cystic fibrosis treatment in the UK and Europe
Cystic fibrosis is an inherited lifelong disease that gets worse over time. It is estimated to affect 105,000 people worldwide. There are more than 2,000 known mutations in the CFTR gene ...