What Is Duchenne Muscular Dystrophy? Muscular dystrophies are ... Scientists continue to look for new ways to treat DMD in clinical trials. These trials test new drugs to see if they are safe ...

offering new pathways for understanding and treating Duchenne Muscular Dystrophy (DMD). A groundbreaking study has shed light on the complex interactions between dystrophin, a protein critical to ...

offering new pathways for understanding and treating Duchenne Muscular Dystrophy (DMD). DMD, a severe genetic disorder that causes muscle weakness and shortens lifespans, arises from mutations in ...

(RTTNews) - Solid Biosciences Inc. (SLDB), a biotechnology company focused on gene therapies for neuromuscular and cardiac diseases, announced the dosing of the first patient in its Phase 1/2 ...

Just a few weeks after Avidity Biosciences made a stir with new data on its experimental therapy for Duchenne muscular dystrophy ... as it has other clinical-stage projects on the go, including ...

The Shanghai-based firm will test the gene therapy candidate in patients between 4 and 9 years old with Duchenne muscular dystrophy.

New therapies for skeletal muscle degeneration are moving into clinical ... of muscular dystrophy, genetic testing is sufficient. Dystrophic muscle biopsy samples show the following features ...

WASHINGTON, Jan. 15, 2025 /PRNewswire/ -- Parent Project Muscular Dystrophy ... in Duchenne, innovations in care including newborns, infants, and toddlers, and updates in clinical research ...

When Raniya Scott was just two years old, her world changed with an unexpected diagnosis: Duchenne muscular dystrophy (DMD), ...

The most commonly reported side effects were cushingoid features, vomiting ... which was investigated in a pivotal study in patients with Duchenne muscular dystrophy (DMD) as an alternative to ...

Muscular dystrophy is caused by defects in certain genes, with type determined by the abnormal gene. In 1986, researchers discovered the gene that, when defective or flawed, causes Duchenne ...