After Sarepta reported the death of a patient who had recently taken the gene therapy Elevidys, patient advocacy group Parent ...
REGENXBIO (RGNX) reported new, positive interim data from two additional patients in the Phase I/II portion of the AFFINITY DUCHENNE trial of ...
A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...
A patient has died while taking a closely watched gene therapy for muscular dystrophy. Sarepta Therapeutics announced the ...
The rapid development of gene therapy options for treating neuromuscular diseases has created new therapeutic options but ...
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