An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

After Sarepta reported the death of a patient who had recently taken the gene therapy Elevidys, patient advocacy group Parent ...

A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...

Sarepta Therapeutics said that a young man died after receiving Elevidys, its gene therapy for Duchenne muscular dystrophy ...

Duchenne muscular dystrophy (DMD) is a genetic condition ... Each time a person who is a carrier of DMD has a child who is assigned male at birth, the child has a 50% chance of developing DMD.