DALLAS—The careful optimization of diet and physical therapy is critical for the care of patients with neuromuscular diseases such as Duchenne muscular ... challenges in pediatric obesity. Oral ...

House Bill 1879 passed unanimously March 4 on a 95-0 vote, according to the chamber's website. State senators will now ...

This article talks about what to expect at your 12-week ultrasound, its importance, and why there are relatively no risks to you or your child. It also explains ... specific risks to the fetus like ...

After Sarepta reported the death of a patient who had recently taken the gene therapy Elevidys, patient advocacy group Parent ...

there are rare cases of spontaneous mutations of the DMD in children whose birth mothers are not carriers of the condition. How Is Duchenne Muscular Dystrophy Diagnosed? DMD is diagnosed through a ...

A patient has died while taking a closely watched gene therapy for muscular dystrophy. Sarepta Therapeutics announced the ...

A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...

Learning from examples like congenital heart disease and cystic fibrosis can help health systems and clinicians prepare to care for an influx of patients with neuromuscular diseases as they reach ...

Sarepta Therapeutics said that a young man died after receiving Elevidys, its gene therapy for Duchenne muscular dystrophy ...

Duchenne muscular dystrophy (DMD) is a genetic condition ... Each time a person who is a carrier of DMD has a child who is assigned male at birth, the child has a 50% chance of developing DMD.

In 2023, Elevidys received expedited U.S. approval despite concerns from some Food and Drug Administration scientists about its effectiveness in treating Duchenne muscular dystrophy. It’s the ...