Art and science are disciplines that have historically co-existed as polarised entities. However, artists and scientists both ...

Laromestrocel (Lomecel-B™) has received FDA Regenerative Medicine Advanced Therapy (RMAT) designation for Alzheimer’s disease which provides frequent interactions with the FDA, intensive guidance on ...

Jack Maina has Gitelman’s syndrome, one of the hardest conditions to diagnose. To this day when he goes for check-ups in ...

Most people exposed to the parasites behind babesiosis don't get sick, but for others, the infection can be deadly.

In an early-stage clinical trial, the therapy nearly doubled the expected survival time of young patients. Still, experts ...

The myelofibrosis drug landscape has become more crowded since Syntara decided to focus on the disease in 2020, but the ...

Rare diseases affect one in 17 people in the UK, but a Government initiative designed to improve their quality of life will ...

A rare disease in the US is one in 1,500, or fewer than 200,000 people, and an ultra-rare disease is one in 50,000 or fewer than than 6,000 people.

PFIC is a group of rare genetic diseases that cause a digestive fluid called bile to accumulate in the liver (pictured in orange above), resulting in extensive damage that often necessitates a ...

Factor XI deficiency is a rare bleeding disorder. People with Factor XI deficiency don’t have enough of a protein in the blood called factor XI. Factor XI is a clotting factor. It is one of the ...

“James was a humanitarian at heart, but also very ... s rare antibodies were crucial in developing Anti-D, the treatment that has protected millions of newborns from Rhesus disease (or ...