Duchenne muscular dystrophy (DMD) is a fatal genetic disorder caused by mutations in the DMD gene. Here, the authors develop MyoAAV-UA, a compact utrophin activator, as a promising universal ...
In this paper, we extend the loop-inspired method from single modal to multiple modals, and from cognitive functions to brain diseases. In the next section, we will introduce how to realize a ...
Aside from muscular dystrophy, other examples of rare diseases include hemophilia, an inherited blood disorder that causes excessive bleeding and bruising; phenylketonuria, an inherited disorder ...
Emerging research indicates that R-loops contribute to the pathogenesis of various disorders, including neurodegenerative, immune-related, and neoplastic diseases. This review summarizes R-loop ...
A postfire debris flow (PFDF) fan covers California State ... products such as models for rapidly assessing debris flow volume and runout. These products can, in turn, help guide efforts to ...
Background Impaired cough results in airway secretion retention, atelectasis and pneumonia in individuals with Duchenne muscular dystrophy (DMD). Lung volume recruitment (LVR ... and peak cough flow.