Vega Gómez, la niña de Zaragoza que sufría una enfermedad rara, ha fallecido a los tres años de edad. La trágica noticia la ...
La niña fue diagnosticada de una enfermedad ultra rara a los nueve meses, la Gangliosidosis GM1 infantil, de la que solo ...
Vega Gómez, la pequeña zaragozana, de 3 años de edad, diagnosticada con Gangliosidosis GM1 infantil, ha fallecido en Zaragoza ...
Company’s lead asset, nizubaglustat, awarded GM1 Orphan Drug Designation by the US Food and Drug administration (FDA) and Orphan Medicinal Product Designation by the European Medicines Agency (EMA) ...
GM1 Gangliosidosis, Krabbe Disease, Alpha1-Antitrypsun deficiency, and solid tumors. The company was founded in 2017 and is headquartered in Bethesda, Maryland.
Acetylleucine (IB-1001) is under development for the treatment of Niemann-Pick disease type C, GM1 Gangliosidosis, GM2 gangliosidosis, ataxia telangiectasia, spinocerebellar ataxia, Tay-Sachs Disease, ...
Acetylleucine (IB-1001) is under development for the treatment of Niemann-Pick disease type C, GM1 Gangliosidosis, GM2 gangliosidosis, ataxia telangiectasia, spinocerebellar ataxia, Tay-Sachs Disease, ...
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