Hunter syndrome can be diagnosed using the physical symptoms of children at the age of 18 months and 4 years. Treatments can help manage condition, no known cure Diagnosed by medical professional ...
Several companies—including JCR Pharmaceuticals, Denali Therapeutics and Regenxbio— have products in the pipeline that could ...
A case of Hunter syndrome, 6½-year-old boy presented with persistent thrombocytopenia and bleeding diathesis. However, cytopenia is not a usual presentation in patients with mucopolysaccharidosis II.
Introduction/purpose Bow Hunter's syndrome is an unusual symptomatic vertebral artery syndrome resulting from intermittent mechanical compression of the vertebral artery. We describe a case of ...
Hunter syndrome affects over 2,000 individuals ... demonstrating positive effects on evidence-based surrogate endpoints and early signs of improved clinical outcomes. Denali's Chief Medical ...
with positive effects on evidence-based surrogate endpoints and early signs of improved clinical outcomes in participants with Hunter syndrome. This designation will provide Denali with more ...